Orphan Disease Center University of Pennsylvania

The Orphan Disease Center University of Pennsylvania is a research center based in Philadelphia, Pennsylvania. With a small team of three employees, the center is dedicated to advancing the treatment and cure of rare diseases. The Orphan Disease Center focuses on developing transformative therapies for orphan diseases, leveraging platform technologies that can be applied across multiple disorders. They prioritize conditions with substantial unmet needs, regardless of their incidence, and aim to ensure accessibility for patients from all backgrounds. The center distinguishes itself through its unique programs, collaborations, and resources. It partners with patient groups, foundations, pharmaceutical and biotech companies, and the academic community. The Orphan Disease Center offers grants, Programs of Excellence, JumpStart programs, and various initiatives to support therapeutic development for rare diseases. For inquiries or further information, visit their website at orphandiseasecenter.med.upenn.edu.